Genetic VectorsGenetic TherapyRNA InterferenceRNA, Small InterferingLentivirusTransduction, GeneticGene Transfer TechniquesX-Linked Combined Immunodeficiency DiseasesRetroviridaeHematopoietic Stem CellsRNATransgenesAdenosine DeaminaseSevere Combined ImmunodeficiencyDependovirusRNA, ViralAdenoviridaeHematopoietic Stem Cell TransplantationRNA, MessengerRNA EditingAntigens, CD34RNA SplicingTransfectionRNA, Double-StrandedGene SilencingCell LineCell Line, TumorRNA, RibosomalBase SequenceMolecular Sequence DataRNA, BacterialGene ExpressionCells, CulturedGene Expression RegulationReverse Transcriptase Polymerase Chain ReactionGreen Fluorescent ProteinsDNA-Directed RNA PolymerasesPromoter Regions, GeneticRNA VirusesHeLa CellsGene Knockdown TechniquesInsect VectorsRNA, CatalyticSignal TransductionDown-RegulationBlotting, WesternTranscription, GeneticRNA, AntisenseApoptosisPlasmidsGenes, ReporterMutationRNA Polymerase IICell ProliferationRNA FoldingRNA StabilityRNA HelicasesGene Expression ProfilingRNA, FungalRNA Processing, Post-TranscriptionalGene TargetingMice, Inbred C57BLDNA PrimersVirusesVirus ReplicationRNA, UntranslatedTime FactorsProtein BindingAmino Acid SequenceNucleic Acid ConformationTranscription FactorsCell SurvivalRNA PrecursorsRNA, Small NuclearRNA, TransferCell DifferentiationGenetic EngineeringLuminescent ProteinsUp-RegulationMice, NudeRNA, ProtozoanRNA, PlantPhosphorylationGene Expression Regulation, NeoplasticSequence Analysis, RNAGenes, Transgenic, Suicidebeta-GalactosidaseModels, BiologicalRNA CapsDisease Models, AnimalDisease VectorsDNANuclear ProteinsMicroscopy, FluorescenceTumor Cells, CulturedDEAD-box RNA HelicasesMice, Inbred BALB CRecombinant Fusion ProteinsPolymerase Chain ReactionThymidine Kinase