Mucopolysaccharidosis IMucopolysaccharidosis VIMucopolysaccharidosis VIIMucopolysaccharidosis IIIMucopolysaccharidosis IIMucopolysaccharidosesMucopolysaccharidosis IVIduronidaseN-Acetylgalactosamine-4-SulfataseChondro-4-SulfataseIduronate SulfataseChondroitinsulfatasesEnzyme Replacement TherapyGlucuronidaseGlycosaminoglycansSulfatasesLysosomesAcetylglucosaminidaseStomatognathic SystemLysosomal Storage DiseasesEnzyme TherapyGenetic TherapyCat DiseasesIduronic AcidKluver-Bucy SyndromeGenetic VectorsDermatan SulfateDisease Models, Animalalpha-MannosidosisCatsFibroblastsbeta-N-AcetylhexosaminidasesMultiple Sulfatase Deficiency DiseaseMouth BreathingMatrix Metalloproteinase 12DogsMucolipidosesHeparitin SulfateGene Transfer TechniquesNeonatal ScreeningMeningesReceptor, IGF Type 2Dog DiseasesPhenotypeDependovirusFaciesGangliosidosesTunisiaMice, Mutant StrainsLiverHyaluronoglucosaminidaseRetroviridaeHydrolasesRecombinant ProteinsKeratan SulfateBrainLeukocytesHeterozygoteFabry DiseaseBase SequenceBlood Specimen CollectionTransduction, GeneticGlycoside HydrolasesMutationJointsCentral Nervous SystemHomozygotePolymerase Chain ReactionAnimals, NewbornMolecular Sequence DataBone and BonesFatal OutcomeMutation, MissenseConsanguinityFrameshift MutationInjections, SpinalDNA Mutational AnalysisBone Marrow TransplantationSpleenPedigreeMice, KnockoutSkinInfant, NewbornDNA PrimersMicroscopy, ElectronInjections, IntravenousTissue DistributionCHO CellsMice, Inbred C57BLHematopoietic Stem Cell TransplantationCells, CulturedCricetinaeBlood-Brain BarrierPoint Mutation