Orphan Drug ProductionRare DiseasesDrug ApprovalEconomics, PharmaceuticalLegislation, DrugUnited States Food and Drug AdministrationDrug IndustryTropical MedicineEthics, PharmacyOff-Label UsePatents as TopicFinancing, OrganizedUnited StatesEuropean UnionResearch Support as TopicDrug CostsTerminology as TopicInsurance, Health, ReimbursementMarketingPharmacologyCost ControlInsurance, Pharmaceutical ServicesChild, OrphanedEuropeResearchFinancing, GovernmentMolecular Sequence Data