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  • symptoms
  • The signs and symptoms of spinal muscular atrophy type 2 (SMA II) typically become apparent between 6 and 12 months of age. (nih.gov)
  • For information about the signs and symptoms of spinal muscular atrophy in general, click here . (nih.gov)
  • Affected people who have extra copies of SMN2 may, therefore, have milder symptoms and develop the condition later in life. (nih.gov)
  • Information from this study, which is part of the NINDS Pilot Therapeutics Network (NPTUNE), may be used for future studies to determine if sodium phenylbutyrate is effective for treating SMA, and if the drug has an effect on SMA symptoms. (clinicaltrials.gov)
  • Currently, no cure exists for spinal muscular atrophy, and treatment is directed towards managing common symptoms of SMA. (stockguru.com)
  • diseases
  • Furthermore, government incentives for development of therapeutic alternatives for rare diseases also boosts research and development in the SMA landscape.Companies with potential candidates in the spinal muscular atrophy pipeline include AveXis, Inc., Cytokinetics, Inc., F. Hoffmann-La Roche Ltd., Novartis AG, and Isis Pharmaceuticals, Inc. (stockguru.com)
  • Phase
  • Albany - NY, Oct. 20, 2015 (GLOBE NEWSWIRE) - According to a new market report published by Transparency Market Research Spinal Muscular Atrophy Market: Pipeline Assessment, Size, Growth, Trends, and Forecast, 2015 - 2023″ the spinal muscular atrophy market phase three candidate ISIS-SMNRx is expected to generate total revenue of USD 0.47 billion by 2023. (stockguru.com)